Research
Read how they describe their research on their Queen's University profile.
Latest papers
Translational insights from nonclinical studies of AAV gene therapies for hemophilia: mechanisms underpinning variability and durability of gene expression.
Therapeutic advances in hematology · 2026 · first author
Evaluation of early prophylactic corticosteroid administration on early safety and efficacy outcomes of adeno-associated virus gene therapy in the hemophilia dog model.
Journal of thrombosis and haemostasis : JTH · 2026
BMN 349, a small molecule inhibitor of Z alpha-1 antitrypsin polymerization, increases secretion and reduces intrahepatic inclusions in a mouse model of disease.
Hepatology (Baltimore, Md.) · 2026
5 publications.
Translational insights from nonclinical studies of AAV gene therapies for hemophilia: mechanisms underpinning variability and durability of gene expression.
Fong S, Swystun LL, Batty P, Lillicrap D
Evaluation of early prophylactic corticosteroid administration on early safety and efficacy outcomes of adeno-associated virus gene therapy in the hemophilia dog model.
Batty P, Swystun LL, Handyside B, Menard A, Harpell L, Hurlbut D, Ismail AM, Mo A, Pender A, Brennan S, Winterborn A, Yates B, Fong S, Lillicrap D
BMN 349, a small molecule inhibitor of Z alpha-1 antitrypsin polymerization, increases secretion and reduces intrahepatic inclusions in a mouse model of disease.
Handyside B, Wenzel H, Mackenzie D, Chang C, Greenslade A, Van Vleet J, Heglar B, Chen JC, Zhang L, Larimore K, Zhou H, Trantcheva I, Sims L, Evans K, Fong S, Kumar G, Annu K, Ronzoni R, Irving JA, Wang B, Bunting S, Lomas DA
Adeno-associated virus-based gene therapy for hemophilia-addressing the gaps.
Miesbach W, Batty P, Chowdary P, Fong S, Kaczmarek R, Leebeek FWG, Long B, Mahlangu J, Makris M, Pierce GF, Pipe SW, Srivastava A, Voorberg J, Peyvandi F
Vector integration and fate in the hemophilia dog liver multiple years after AAV-FVIII gene transfer.
Batty P, Fong S, Franco M, Sihn CR, Swystun LL, Afzal S, Harpell L, Hurlbut D, Pender A, Su C, Thomsen H, Wilson C, Youssar L, Winterborn A, Gil-Farina I, Lillicrap D
Frequent collaborators
- David Lillicrap and Paul Batty: 10 shared papers
- David Lillicrap and Sylvia Fong: 3 shared papers
- Paul Batty and Sylvia Fong: 3 shared papers
- David Lillicrap and David Hurlbut: 2 shared papers
- Paul Batty and David Hurlbut: 2 shared papers
- Sylvia Fong and David Hurlbut: 2 shared papers
- Pathology
- Department of Medicine
Co-authors at Queen's University, colored by department. Thicker lines mean more shared papers; select anyone to open their profile and their own map.
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Profile data last refreshed on September 29, 2026 from the university directory, publication records and public research funding records.